Development of an in vitro model of dysferlinopathy via crispr/cas-mediated transcriptional activation of the dysf gene
- Authors: Yakovlev I.A.1,2, Slesarenko Y.S.2, Starostina I.G.3, Shaimardanova A.A.3, Solovyova V.V.3, Bobrovsky P.A.4, Grafskaia E.N.4, Belikova L.D.4, Bardakov S.N.1, Rizvanov A.A.3,5, Isaev A.A.1, Deev R.V.1,2,6
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Affiliations:
- Artgene Biotech
- OOO Genotarget, Skolkovo Innovation Center
- Kazan (Volga Region) Federal University
- Lopukhin Federal Research and Clinical Center of Physical-Chemical Medicine
- Division of Medical and Biological Sciences, Tatarstan Academy of Sciences
- Avtsyn Research Institute of Human Morphology, Petrovsky National Research Centre of Surgery
- Issue: Vol 66, No 4 (2024)
- Pages: 380-392
- Section: Articles
- URL: https://ruspoj.com/0041-3771/article/view/669502
- DOI: https://doi.org/10.31857/S0041377124040064
- EDN: https://elibrary.ru/QCPXOW
- ID: 669502
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